The 8th of March Was a historic day!
We are so happy to announce that NHSE and Novartis Gene have reached an agreement which will enable families in England to have access to gene therapy for Spinal Muscular Atrophy - one of the most expensive treatments in England on the NHS.
This was our first sitting on a panel when approving a drug along with two other SMA Charities, stakeholders and professionals.
Like Spinraza there will be stipulations as to who can receive it. Please read further by clicking here

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